Rare Disease Advisor, a trusted source of medical news and feature content for healthcare providers, offers clinicians insight into the latest research to inform clinical practice and improve patient ...

Consolidation or maintenance therapy significantly improved progression-free survival and overall survival. Zanubrutinib, lenalidomide, temozolomide, and rituximab (RLZT) combined with or without high ...

Meta-analysis estimates global PPF incidence at 10.9/100,000 and prevalence at 37/100,000, rarer in Europe and Asia but higher in the US. The pooled global incidence and prevalence of progressive ...

As winter sets in, many people enjoy a hot mug of cocoa, snuggly sweaters, and outdoor activities such as walking through town to watch the lighting of the town tree or skiing with friends. There are ...

The model had an area under the receiver operating characteristic curve of 0.83 in a high-risk subgroup of patients with conditions that mimic ATTR-CM. An artificial intelligence model trained to ...

This is a multicenter, randomized, double-blind, placebo-controlled study to evaluate the efficacy and safety of IMVT-1402 in adult participants with active CIDP. A new clinical trial (NCT07032662) to ...

Larry Luxner, senior correspondent for Rare Disease Advisor, talks with Claire Booth, MBBS, PhD, of University College London in the UK and cofounder of the AGORA Initiative, which aims to tackle the ...

Taylor Kane is executive director of Remember the Girls, a nonprofit group that advocates on behalf of females with X-linked disorders (Photo courtesy of Taylor Kane) New Jersey native Taylor Kane ...

Claseprubart incorporates YTE half-life extension technology, which is designed to enable infrequent subcutaneous self-administration. A phase 3 study is underway to evaluate the investigational ...

The CAPTIVATE trial met its target of at least 20 responders among the first 40 participants before all 40 completed part A. Dianthus Therapeutics announced an early “go” decision for claseprubart for ...

Neuraxial anesthesia was successfully administered for cesarean delivery in 58 of 64 cases analyzed. Neuraxial anesthesia is emerging as a potentially safe and effective option in patients with ...

Successful treatment involving spesolimab rapid induction and secukinumab maintenance therapy was reported recently in a 62-year-old female patient with annular GPP. In patients with annular ...